SRP-9003 rAAVr74.MCK.SCGB Gene Therapy for Limb Girdle Dystrophy (Sarepta Therapeutics): Clinical Study Update

Gene Therapy for Phenylketonuria: Homology & Biomarin Race to Bring Single Dose Treatment To Market

Self-Complementary Adeno Associated Virus (scAAV) Vector Design For Efficient Gene Delivery

CRIM Status, Genotype, Residual Enzyme Activity and Immunogenicity (Unwanted Immune Response)

Voyager Therapeutics: Overview of Clinical Stage Pipeline

Gene Therapy for Parkison Disease: RESTORE-1 NBIb-1817 (VY-AADC) Clinical Update

Gene Therapy for LCA10: The Brilliance Phase 1/2 Clinical Trial Of AGN-151587 (EDIT-101) Update

Homology Therapeutics, HMI-102 (Gene-therapy) in adult subjects with Phenylketonuria (PKU)

Targeted Enrichment & Mutation Analysis using Illumina Sequencing Platform (Short Reads ~300 bps)

T-cell Response After Administration of AVVrh74.MHCK7 For Duchenne Muscular Dystrophy: Result from Open Labeled Control Trial

Sangamo/Pfizer's Giroctocogene Fitelparvovec Gene Therapy for Hemophilia- Clinical Update

AAVrh74.MHCK7.micro-dystrophin (Serapta Therapeutics)- SRP- 9001 for Duchenne Muscular: Update From Phase 2 Clinical Studies

AVV9-minidystrophin (Pfizer- PF-06939926) for Duchenne Muscular Dystrophy: Clinical Study Update

AAV9- microdystrophin (Solid Biosciences- SGT-001 ) For Duchenne Muscular Dystrophy Treatment: Update on Clinical Studies

Caribou Biosciences: Overview of Clinical Stage Pipeline

Homology Medicine: Overview of Clinical Stage Pipeline

Editas Medicine: Overview of Clinical Stage Pipeline

Analytical Platform Review: FPLC and UHPLC For Protein Purification and Characterization