Clinical Trial Design for Cellular and Gene Therapy

Why UniQure's Etranacogene dezaparvovec Gene Therapy Still Holds A Promise For Hemophilia B Patients With Unmet Medical Needs

Uniqure hemophilia B gene therapy program On Clinical hold by the U.S. Food and Drug Administration (FDA)

Uniqure: Portfolio, Stock & Financial Analysis

Homology Medicine Growth Rely On Successful Phenylketonuria (PKU) Gene Therapy Program

Beam Therapeutics (Nasdaq: BEAM) Portfolio, Stock and Growth

Orchard Therapeutics: European Medicines Approves Libmeldy™ for the Treatment of Early-Onset Metachromatic Leukodystrophy (MLD)

Orchard Therapeutics: Clinical Study on Gene Therapy for Metachromatic Leukodystrophy (MLD)

Orchard Therapeutics: Clinical Study on Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IIIA

Bluebird Bio's: Lentiglobulin Infusion Showed Durable Expression of Modified Form Functional Beta-Globin in Sickle Cell Disease

CTX001: CRISPR Therapeutics and Vertex Present Positive Clinical Data for Investigational Gene-Editing Therapy CTX001™ in Severe Hemoglobinopathies

Three Hot CRISPR based Gene Editing Companies ( CRSP, EDIT, NTLA)

Step Wise Protocol For Preparation of Adeno-Associated Virus Luciferase Stock

Labeling and Visualization of Endoplasmic reticulum using ER Tracker

Labeling and Visualization of Lysosome using Lysotracker

Antibodies For Lysosomal LAMP1 Protein Western Blot Analysis & Immunofluorescence Staining

Easy-to-Follow Protocol For Western Blot Analysis & Immunofluorescence Staining

Gene Therapy for Sickle Cell Disease: Competitive Landscape, Clinical Development Programs

DNA Extraction Kits from Blood & Tissues

Quantification of Adeno-Associated Viral Vectors by Digital Droplet PCR

Adverse Events: Introduction and FDA Reporting Requirements for IND studies