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SRP-9003 rAAVr74.MCK.SCGB Gene Therapy for Limb Girdle Dystrophy (Sarepta Therapeutics): Clinical Study Update

Gene Therapy for Phenylketonuria: Homology & Biomarin Race to Bring Single Dose Treatment To Market

AAV5-PAH Gene Therapy Clinical Study for Subjects With Phenylketonuria: Update

Self-Complementary Adeno Associated Virus (scAAV) Vector Design For Efficient Gene Delivery

CRIM Status, Genotype, Residual Enzyme Activity and Immunogenicity (Unwanted Immune Response)

Voyager Therapeutics: Overview of Clinical Stage Pipeline

Gene Therapy for Parkison Disease: RESTORE-1 NBIb-1817 (VY-AADC) Clinical Update

Gene Therapy for LCA10: The Brilliance Phase 1/2 Clinical Trial Of AGN-151587 (EDIT-101) Update

Homology Therapeutics Clinical Study Update on HMI-102 (Gene-therapy) in adult subjects with Phenylketonuria (PKU)

Long-Read Sequencing Technology To Investigate Viral Vector Integration into Host Genome

Targeted Enrichment & Mutation Analysis using Illumina Sequencing Platform (Short Reads ~300 bps)

T-cell Response After Administration of AVVrh74.MHCK7 For Duchenne Muscular Dystrophy: Result from Open Labeled Control Trial

Update on Valoctocogene Roxaparvovec Gene Therapy for Severe Hemophilia A

Illumina Nextera XT DNA Sequencing Library Preparation Kit

Sangamo/Pfizer's Giroctocogene Fitelparvovec Gene Therapy for Hemophilia- Clinical Update

Gene Therapy for Treatment of Duchenne Muscular Dystrophy: Race to Bring Therapy to Market (Sarepta, Pfizer & Solid Biosciences)

AAVrh74.MHCK7.micro-dystrophin (Serapta Therapeutics- SRP- 9001 for Duchenne Muscular: Update From Phase 2 Clinical Studies

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